The idea of self-amplifying gene editing is to get cells to pass on packages of CRISPR machinery to their neighbours, ...
Scientists are testing an entirely new way to fight heart disease: whether gene editing might offer a one-time fix for high ...
A gene therapy that patients breathe in has been found to shrink lung tumours by inserting immune-boosting genes into ...
Researchers led by Min Zhang and Dabao Zhang of the University of California, Irvine's Joe C. Wen School of Population & ...
Gene regulation is far more predictable than previously believed, scientists conclude after developing the deep learning ...
A new study has confirmed that male and female lungs are "wired differently" at the molecular level, providing further ...
After facing a delayed decision deadline and a clinical hold, Regenxbio’s Hunter syndrome gene therapy has been rejected by ...
The FDA recommended that REGENXBIO run a new study, treat more patients and include a placebo arm to support a resubmission ...
All participants had adverse events, but most were moderate in severity ...
In this webinar, researchers discuss using and improving next-generation gene editing approaches for targeted, accurate, and ...
Gene therapy drugs have the potential to cure some diseases, but some have a price tag of over a million dollars. Who gets access to them and who doesn't?