Sarepta's stock falls 48% after FDA critic Vinay Prasad's appointment and poor Elevidys sales. Company cuts revenue forecast ...

NewLimit raises $130M Series B led by Kleiner Perkins to advance epigenetic reprogramming research for liver disease ...

The FDA on Tuesday said it is planning on doing more surprise inspections of foreign factories, a day after Trump signed an ...

House and Senate lawmakers from both parties are working with the Trump administration on proposals that would use drug ...

Attorneys general from 19 states and Washington, DC have filed a lawsuit against the federal government alleging that its ...

The European Union is committing €500 million ($556 million) over the next two years to make Europe a “magnet” for ...

A Singapore-based startup raised a $45 million Series B to start testing a gene therapy in humans next year for a genetic ...

Vertex said it's gathering momentum with its new product launches, building out new franchises with its sickle cell therapy ...

Several members of an FDA advisory committee warned on Monday that new data from studies on long-term use of opioids might ...

Function Health is buying Ezra in a bid to create a haven for people who want copious amounts of data on their bodies. The ...

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J&J's gene therapy bota-vec failed Phase 3 trial for X-linked retinitis pigmentosa vision loss. Follows trend of big pharma ...